EFPIA - NEWSLETTER

EFPIA Newsletter 02 March 2023

Rare Disease Day

Innovation is delivering therapies for people with rare diseases – but R&D needs...

Investment in R&D in Europe is vital if we are to tackle unmet medical needs.

In this blog, Nathalie Moll, EFPIA Director General, outlines how the story of rare diseases also explains why mindful policymaking and sustained investment are essential to turn science into treatments, and why we must continually renew our commitment to supporting Europe’s research and development eco-system.

How the Rare Disease Moonshot can unlock science for patients

For most rare diseases, there is not enough science to translate into innovative products. It’s time to change this together through public-private collaboration.

Magda Chlebus, Executive Director of Science Policy & Regulatory Affairs at EFPIA, outlines the RD Moonshot as a concrete example of how public and private players, with patients as key partners, can add the momentum needed to advance the care of people with rare diseases.

News

28 February 2023 Because we can’t afford not to - Let’s make a joint health check for cardiovascular disease...

Join us in the European Parliament

09 February 2023 Industry Statement on the earthquakes in Turkey and Syria

Industry will continue to work with partners and authorities across Europe to provide further support where possible....

Blogs

02 March 2023 Dynamic Regulatory Assessment will support more efficient treatment development for patients:...

Regulatory Road to Innovation

01 March 2023 This March we are moving together against Colorectal Cancer! #ECCAM2023

#ECCAM2023 is an opportunity to encourage those eligible for colorectal cancer screening to get screened: early detection...

Events

13 MAR 2023

Women’s Brain Project special webinar Online

Sex, gender and the brain: Towards an inclusive research agenda

Learn more →

16 MAR 2023

GetReal Institute Annual Conference 2023 Utrecht, Netherlands

A European Outlook on Real World Evidence in a Global Context

Learn more →

22 MAR 2023

DIA Europe 2023 - 35th Anniversary of the event Basel, Switzerland

35th Anniversary of the event

Learn more →

30 MAR 2023

The Estimands Academy for Trial Teams: Bringing estimands to life through case studies... Online

Webinar 4 - Proposing Estimands from Different Perspectives: Patient, Clinician, Regulator, Health Technology Assessor...

Learn more →

What we are reading

Gap between EU & US on pharmaceutical investments too wide - industry 28 February 2023 (Euronews)

About the EFPIA newsletter

The European Federation of Pharmaceutical Industries and Associations (EFPIA) represents the pharmaceutical industry operating in Europe. Through its direct membership of 36 national associations and 39 leading pharmaceutical companies, EFPIA is the voice on the EU scene of 1,900 companies committed to researching, developing and bringing to patients new medicines that will improve health and the quality of life around the world.

Tel: +32 (0)2 626 25 55
Communications@efpia.eu

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